Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa

D. Hughes; R. Giugliani; N. Guffon; S. A. Jones; K. E. Mengel; R. Parini; R. Matousek; S. M. Hawley; A. Quartel

doi:10.1186/s13023-017-0634-0

Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa

D. Hughes, R. Giugliani, N. Guffon, S. A. Jones, K. E. Mengel, R. Parini, R. Matousek, S. M. Hawley, A. Quartel

Division of Cell Matrix Biology & Regenerative Medicine (L5)

Research output: Contribution to journal › Article › peer-review

Original language	English
Journal	Orphanet Journal of Rare Diseases
Volume	12
Issue number	1
Early online date	23 May 2017
DOIs	https://doi.org/10.1186/s13023-017-0634-0
Publication status	Published - 1 Dec 2017

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10.1186/s13023-017-0634-0

http://ojrd.biomedcentral.com/articles/10.1186/s13023-017-0634-0

Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa
Hughes, D. (Creator), Giugliani, R. (Creator), Guffon, N. (Creator), Jones, S. (Creator), Mengel, K. (Creator), Parini, R. (Creator), Matousek, R. (Creator), Hawley, S. (Creator) & Quartel, A. (Creator), figshare , 23 May 2017
DOI: 10.6084/m9.figshare.c.3786374
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Cite this

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title = "Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa",

author = "D. Hughes and R. Giugliani and N. Guffon and Jones, {S. A.} and Mengel, {K. E.} and R. Parini and R. Matousek and Hawley, {S. M.} and A. Quartel",

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AU - Hughes, D.

AU - Giugliani, R.

AU - Guffon, N.

AU - Jones, S. A.

AU - Mengel, K. E.

AU - Parini, R.

AU - Matousek, R.

AU - Hawley, S. M.

AU - Quartel, A.

PY - 2017/12/1

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DO - 10.1186/s13023-017-0634-0

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SN - 1750-1172

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JO - Orphanet Journal of Rare Diseases

JF - Orphanet Journal of Rare Diseases

IS - 1

ER -

Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa

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Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa

Cite this