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Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa
Hughes, D. (Creator), Giugliani, R. (Creator), Guffon, N. (Creator), Jones, S. (Creator), Mengel, K. (Creator), Parini, R. (Creator), Matousek, R. (Creator), Hawley, S. (Creator) & Quartel, A. (Creator), figshare , 23 May 2017
DOI: 10.6084/m9.figshare.c.3786374
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